[Gene therapy].

A Fischer; C Schatz

PubMed · 7482391

[Gene therapy].

Abstract

This paper considers the prerequisites for gene therapy. This new field of therapeutics has not yet proved its efficacity nor its safety. Use, as a drug of DNA molecules which can modify host genome and environment as well requires specific prerequisites; among them, animal experimental models are essential despite their limitations. The different preclinical and clinical steps in the design of gene therapy studies are also discussed.

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Animals Clinical Trials as Topic Drug Evaluation, Preclinical France Genetic Therapy Humans In Vitro Techniques English Abstract Journal Article

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A Fischer, C Schatz. [Gene therapy].. https://pubmed.ncbi.nlm.nih.gov/7482391/

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