@misc{indiciae68fedfd73ef4, title = {A First-in-Japanese Phase 1, Double-Blind, Placebo-Controlled, Parallel-Cohort Study of Sefaxersen, an Antisense Oligonucleotide Targeting Complement Factor B, in Healthy Participants.}, author = {Takakazu Sato and Hiroyuki Fukase and Takaaki Ishida and Arisa Karasawa}, year = {2026}, doi = {10.1002/cpdd.70097}, url = {https://pubmed.ncbi.nlm.nih.gov/42713733/}, note = {Source identifier: 42713733} }