@misc{indiciae099a90b77410,
  title = {AAV-mediated CBLN1 replacement rescues hereditary ataxia caused by bi-allelic CBLN1 variants.},
  author = {Tokiwa Yamasaki and Wataru Kakegawa and Ayumi Hayashi and Naoko Ogawa and Tetsuya Takano and Keiko Matsuda and Kumi Takatsuto and Mohamed S Abdel-Hamid and Maha S Zaki and Joseph G Gleeson and Michisuke Yuzaki},
  year = {2026},
  doi = {10.1016/j.ymthe.2026.09.003},
  url = {https://pubmed.ncbi.nlm.nih.gov/42687380/},
  note = {Source identifier: 42687380}
}