@misc{indiciaebf9787a52ca8,
  title = {Peptide-phosphorodiamidate morpholino oligomer therapy for dysferlinopathy induces pseudoexon skipping and restoration of functional protein.},
  author = {James E Gooding and Gyeongsu Park and Atish Wagh and Jonathan K Watts and Janice A Dominov and Robert H Brown},
  year = {2026},
  doi = {10.1172/jci.insight.204742},
  url = {https://pubmed.ncbi.nlm.nih.gov/42446943/},
  note = {Source identifier: 42446943}
}