@misc{indiciae779b0efe07e5, title = {Phase 3 Trial of Oral Infigratinib in Children with Achondroplasia.}, author = {Ravi Savarirayan and Julie Hoover-Fong and Melita Irving and Paul Arundel and Josep Maria de Bergua and Philippe M Campeau and Toby Candler and Benjamin T Cocanougher and Valerie Cormier-Daire and Thomas Edouard and Svein O Fredwall and Paul Harmatz and Daniel Hoernschemeyer and Henrik U Irgens and Saumya Jamuar and Peter Kannu and Janet M Legare and Antonio Leiva-Gea and Helen McDevitt and Roberta Onesimo and John Phillips and Mariana Del Pino and Marie-Eve Robinson and Massimiliano Rossi and Mars Skae and Leanne M Ward and Klane K White and Jane Schmidt and Ted Lystig and Ariana Salvatici and Yun Bai and Peter W Butler and David van Veenhuyzen and Daniela Rogoff}, year = {2026}, doi = {10.1056/nejmoa2604565}, url = {https://pubmed.ncbi.nlm.nih.gov/42370681/}, note = {Source identifier: 42370681} }